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54 results

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Page 1
Sports Injuries in Basketball Players: A Systematic Review.
Aksović N, Bubanj S, Bjelica B, Kocić M, Lilić L, Zelenović M, Stanković D, Milanović F, Pajović L, Čaprić I, Milić V, Dobrescu T, Sufaru C. Aksović N, et al. Among authors: bjelica b. Life (Basel). 2024 Jul 19;14(7):898. doi: 10.3390/life14070898. Life (Basel). 2024. PMID: 39063651 Free PMC article. Review.
Clinical Effectiveness of Newborn Screening for Spinal Muscular Atrophy: A Nonrandomized Controlled Trial.
Schwartz O, Vill K, Pfaffenlehner M, Behrens M, Weiß C, Johannsen J, Friese J, Hahn A, Ziegler A, Illsinger S, Smitka M, von Moers A, Kölbel H, Schreiber G, Kaiser N, Wilichowski E, Flotats-Bastardas M, Husain RA, Baumann M, Köhler C, Trollmann R, Schwerin-Nagel A, Eisenkölbl A, Schimmel M, Fleger M, Kauffmann B, Wiegand G, Baumgartner M, Rauscher C, Cirak S, Gläser D, Bernert G, Hagenacker T, Goldbach S, Probst-Schendzielorz K, Lochmüller H, Müller-Felber W, Schara-Schmidt U, Walter MC, Kirschner J, Pechmann A; SMARTCARE study group. Schwartz O, et al. JAMA Pediatr. 2024 Jun 1;178(6):540-547. doi: 10.1001/jamapediatrics.2024.0492. JAMA Pediatr. 2024. PMID: 38587854 Free PMC article. Clinical Trial.
Efficacy and safety of gene therapy with onasemnogene abeparvovec in children with spinal muscular atrophy in the D-A-CH-region: a population-based observational study.
Weiß C, Becker LL, Friese J, Blaschek A, Hahn A, Illsinger S, Schwartz O, Bernert G, Hagen MV, Husain RA, Goldhahn K, Kirschner J, Pechmann A, Flotats-Bastardas M, Schreiber G, Schara U, Plecko B, Trollmann R, Horber V, Wilichowski E, Baumann M, Klein A, Eisenkölbl A, Köhler C, Stettner GM, Cirak S, Hasselmann O, Kaindl AM, Garbade SF, Johannsen J, Ziegler A; SMArtCARE and Swiss-Reg-NMD study group. Weiß C, et al. Lancet Reg Health Eur. 2024 Oct 7;47:101092. doi: 10.1016/j.lanepe.2024.101092. eCollection 2024 Dec. Lancet Reg Health Eur. 2024. PMID: 39434961 Free PMC article.
Long-Term Dynamics of CSF and Serum Neurofilament Light Chain in Adult Patients With 5q Spinal Muscular Atrophy Treated With Nusinersen.
Cordts I, Fuetterer C, Wachinger A, von Heynitz R, Kessler T, Freigang M, Quinten AL, Bjelica B, Brakemeier S, Hobbiebrunken E, Hagenacker T, Petri S, Koch JC, Hahn A, Lingor P, Deschauer M, Günther R, Weiler M, Haller B, Feneberg E. Cordts I, et al. Among authors: bjelica b. Neurology. 2025 Mar 11;104(5):e213371. doi: 10.1212/WNL.0000000000213371. Epub 2025 Feb 13. Neurology. 2025. PMID: 39946662 Free PMC article.
Dextromethorphan/quinidine (DMQ) for reducing bulbar symptoms in amyotrophic lateral sclerosis - assessment of treatment experience in a multicenter study.
Spittel S, Grehl T, Weydt P, Kettemann D, Fabian R, Rödiger A, Smesny U, Steinbach R, Ilse B, Weyen U, Petri S, Lumi R, Bjelica B, Lingor P, Grosskreutz J, Göricke BM, Pfeilschifter W, Schmeja W, Dorst J, Mensch A, Siebert J, Norden J, Bernsen S, Subramanian SK, Hildebrandt B, Walter B, Münch C, Maier A, Meyer T. Spittel S, et al. Among authors: bjelica b. Amyotroph Lateral Scler Frontotemporal Degener. 2025 Sep 11:1-13. doi: 10.1080/21678421.2025.2557932. Online ahead of print. Amyotroph Lateral Scler Frontotemporal Degener. 2025. PMID: 40932199 Free article.
Respiratory function in 192 adult patients with spinal muscular atrophy (SMA) treated with nusinersen - a multicenter observational study.
Wurster CD, Stolte B, Kessler T, Freigang M, Bjelica B, Ilse B, Koch JC, Cordts I, Mensch A, Zeller D, Uzelac Z, Sam G, Lapp HS, Wohnrade C, Rödiger A, Muhandes MT, Schneider I, Bellut J, Nentwich J, Dorst J, Schuster J, Schreiber-Katz O, Osmanovic A, Totzeck A, Thimm A, Steinbach R, Grosskreutz J, Kleinschnitz C, Ludolph AC, Deschauer M, Kirschner J, Dreyhaupt J, Wollinsky K, Petri S, Weiler M, Hagenacker T, Günther R. Wurster CD, et al. Among authors: bjelica b. Orphanet J Rare Dis. 2025 Sep 8;20(1):476. doi: 10.1186/s13023-025-04009-3. Orphanet J Rare Dis. 2025. PMID: 40922023 Free PMC article.
54 results