Investigational eIF2B activator DNL343 modulates the integrated stress response in preclinical models of TDP-43 pathology and individuals with ALS in a randomized clinical trial.
Flores BN, Yu SB, Cohen IV, Fanok MH, Luan W, Maciuca RD, Sun LD, Tsai RM, Vissers M, Smits L, Bunte TM, Bakardjiev A, Balasundar S, Calvert MEK, Chin MY, Dobbins SK, Dowdle WE, Fang M, Heuberger JAAC, Ha CL, Huang F, Miyamoto T, Osipov M, Madrid San Martin L, Saund K, Tatarakis D, Vu AQ, Xiong C, Yeo GW, Groeneveld GJ, van den Berg LH, Dhuria S, Estrada AA, Jennings D, Sandmann T, Ho C, Scearce-Levie K, Yulyaningsih E, Walker AK, Di Paolo G, Kane LA, Troyer MD, Lewcock JW.
Flores BN, et al. Among authors: bunte tm.
Nat Commun. 2025 Aug 18;16(1):7690. doi: 10.1038/s41467-025-63031-y.
Nat Commun. 2025.
PMID: 40825784
Free PMC article.
Clinical Trial.