First real-world study of fetal therapy with CFTR modulators in cystic fibrosis: Report from the MODUL-CF study.
Bonnel AS, Bihouée T, Ribault M, Driessen M, Grèvent D, Foissac F, Truong NH, Benhamida M, Arnouat B, Borghese R, Chedevergne F, Couderc-Kohen L, da Silva J, Grenet D, Houdouin V, Le A, Marchal S, Deneuville E, Pouradier D, Rousseau V, Treluyer JM, Francart A, Steffann J, Reix P, Benaboud S, Mamzer MF, Ville Y, Martin C, Burgel PR, Sermet-Gaudelus I; MODUL-CF study group.
Bonnel AS, et al. Among authors: francart a.
J Cyst Fibros. 2025 May;24(3):457-465. doi: 10.1016/j.jcf.2025.03.009. Epub 2025 Mar 24.
J Cyst Fibros. 2025.
PMID: 40133101