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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
1997 4
1998 2
1999 3
2000 4
2001 3
2002 6
2003 2
2004 5
2005 5
2006 6
2007 9
2008 6
2009 4
2010 13
2011 20
2012 12
2013 11
2014 6
2015 14
2016 14
2017 13
2018 14
2019 22
2020 25
2021 32
2022 33
2023 19
2024 33
2025 18

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323 results

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Page 1
Betibeglogene Autotemcel Gene Therapy for Non-β0/β0 Genotype β-Thalassemia.
Locatelli F, Thompson AA, Kwiatkowski JL, Porter JB, Thrasher AJ, Hongeng S, Sauer MG, Thuret I, Lal A, Algeri M, Schneiderman J, Olson TS, Carpenter B, Amrolia PJ, Anurathapan U, Schambach A, Chabannon C, Schmidt M, Labik I, Elliot H, Guo R, Asmal M, Colvin RA, Walters MC. Locatelli F, et al. Among authors: hongeng s. N Engl J Med. 2022 Feb 3;386(5):415-427. doi: 10.1056/NEJMoa2113206. Epub 2021 Dec 11. N Engl J Med. 2022. PMID: 34891223 Clinical Trial.
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia.
Thompson AA, Walters MC, Kwiatkowski J, Rasko JEJ, Ribeil JA, Hongeng S, Magrin E, Schiller GJ, Payen E, Semeraro M, Moshous D, Lefrere F, Puy H, Bourget P, Magnani A, Caccavelli L, Diana JS, Suarez F, Monpoux F, Brousse V, Poirot C, Brouzes C, Meritet JF, Pondarré C, Beuzard Y, Chrétien S, Lefebvre T, Teachey DT, Anurathapan U, Ho PJ, von Kalle C, Kletzel M, Vichinsky E, Soni S, Veres G, Negre O, Ross RW, Davidson D, Petrusich A, Sandler L, Asmal M, Hermine O, De Montalembert M, Hacein-Bey-Abina S, Blanche S, Leboulch P, Cavazzana M. Thompson AA, et al. Among authors: hongeng s. N Engl J Med. 2018 Apr 19;378(16):1479-1493. doi: 10.1056/NEJMoa1705342. N Engl J Med. 2018. PMID: 29669226 Free article. Clinical Trial.
Betibeglogene autotemcel gene therapy in patients with transfusion-dependent, severe genotype β-thalassaemia (HGB-212): a non-randomised, multicentre, single-arm, open-label, single-dose, phase 3 trial.
Kwiatkowski JL, Walters MC, Hongeng S, Yannaki E, Kulozik AE, Kunz JB, Sauer MG, Thrasher AJ, Thuret I, Lal A, Tao G, Ali S, Thakar HL, Elliot H, Lodaya A, Lee J, Colvin RA, Locatelli F, Thompson AA. Kwiatkowski JL, et al. Among authors: hongeng s. Lancet. 2024 Nov 30;404(10468):2175-2186. doi: 10.1016/S0140-6736(24)01884-1. Epub 2024 Nov 8. Lancet. 2024. PMID: 39527960 Clinical Trial.
The translational gap for gene therapies in low- and middle-income countries.
Doxzen KW, Adair JE, Fonseca Bazzo YM, Bukini D, Cornetta K, Dalal V, Guerino-Cunha RL, Hongeng S, Jotwani G, Kityo-Mutuluuza C, Lakshmanan K, Mahlangu J, Makani J, Mathews V, Ozelo MC, Rangarajan S, Scholefield J, Batista Silva Júnior J, McCune JM. Doxzen KW, et al. Among authors: hongeng s. Sci Transl Med. 2024 May 8;16(746):eadn1902. doi: 10.1126/scitranslmed.adn1902. Epub 2024 May 8. Sci Transl Med. 2024. PMID: 38718130 Review.
Therapeutic delivery of recombinant glucocerebrosidase enzyme-containing extracellular vesicles to human cells from Gaucher disease patients.
Janpipatkul K, Sutjarit N, Tangprasittipap A, Chaiamarit T, Innachai P, Suksen K, Chokpanuwat T, Tim-Aroon T, Anurathapan U, Jearawiriyapaisarn N, Tubsuwan A, Bowornpinyo S, Asavapanumas N, Chairoungdua A, Bhukhai K, Hongeng S. Janpipatkul K, et al. Among authors: hongeng s. Orphanet J Rare Dis. 2024 Oct 2;19(1):363. doi: 10.1186/s13023-024-03376-7. Orphanet J Rare Dis. 2024. PMID: 39358794 Free PMC article.
Mesenchymal Stromal Cells and Viral Infection.
Thanunchai M, Hongeng S, Thitithanyanont A. Thanunchai M, et al. Among authors: hongeng s. Stem Cells Int. 2015;2015:860950. doi: 10.1155/2015/860950. Epub 2015 Jul 29. Stem Cells Int. 2015. PMID: 26294919 Free PMC article. Review.
Genomics-Driven Precision Medicine in Pediatric Solid Tumors.
Suthapot P, Chiangjong W, Chaiyawat P, Choochuen P, Pruksakorn D, Sangkhathat S, Hongeng S, Anurathapan U, Chutipongtanate S. Suthapot P, et al. Among authors: hongeng s. Cancers (Basel). 2023 Feb 23;15(5):1418. doi: 10.3390/cancers15051418. Cancers (Basel). 2023. PMID: 36900212 Free PMC article. Review.
Mitapivat in adults with non-transfusion-dependent α-thalassaemia or β-thalassaemia (ENERGIZE): a phase 3, international, randomised, double-blind, placebo-controlled trial.
Taher AT, Al-Samkari H, Aydinok Y, Besser M, Boscoe AN, Dahlin JL, De Luna G, Estepp JH, Gheuens S, Gilroy KS, Glenthøj A, Sim Goh A, Iyer V, Kattamis A, Loggetto SR, Morris S, Musallam KM, Osman K, Ricchi P, Salido-Fiérrez E, Sheth S, Tai F, Tevich H, Uhlig K, Urbstonaitis R, Viprakasit V, Cappellini MD, Kuo KHM; ENERGIZE investigators. Taher AT, et al. Lancet. 2025 Jul 5;406(10498):33-42. doi: 10.1016/S0140-6736(25)00635-X. Epub 2025 Jun 19. Lancet. 2025. PMID: 40544857 Clinical Trial.
323 results