Epidemiology of Gaucher Disease in France: Trends in Incidence, Mortality, Management, and Complications Over Three Decades.
Nguyen Y, Beydon M, Yousfi K, Zebiche S, Hamroun D, Brassier A, Pichard S, Swiader L, Billette de Villemeur T, Héron B, Dalbies F, Cador B, Guemann AS, Gaches F, Hivert B, Leguy-Seguin V, Masseau A, Deshayes R, Pers YM, Pettazzoni M, Bekri S, Caillaud C, Le Guillou E, Szymanowski M, Astudillo L, Mauhin W, Nadjar Y, Serratrice C, Berger MG, Camou F, Belmatoug N, Stirnemann J; French Evaluation of Gaucher Disease Treatment Committee.
Nguyen Y, et al. Among authors: leguy seguin v.
J Inherit Metab Dis. 2025 May;48(3):e70037. doi: 10.1002/jimd.70037.
J Inherit Metab Dis. 2025.
PMID: 40348574
Free PMC article.