Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation

Search Page

Filters

My Custom Filters

Results by year

Table representation of search results timeline featuring number of search results per year.

Year Number of Results
1960 1
1964 1
1974 1
1978 1
1980 2
1981 1
1985 3
1986 1
1988 4
1992 1
1993 1
1994 1
1996 2
1997 1
1998 6
1999 9
2000 10
2001 9
2002 5
2003 8
2004 6
2005 12
2006 11
2007 11
2008 9
2009 17
2010 14
2011 10
2012 7
2013 4
2014 11
2015 10
2016 5
2017 4
2018 2
2019 2
2020 1
2021 5
2022 3
2023 5
2024 3
2025 7

Publication date

Text availability

Article attribute

Article type

Additional filters

Article Language

Species

Sex

Age

Other

Search Results

211 results

Results by year

Filters applied: . Clear all
Page 1
In vivo editing of lung stem cells for durable gene correction in mice.
Sun Y, Chatterjee S, Lian X, Traylor Z, Sattiraju SR, Xiao Y, Dilliard SA, Sung YC, Kim M, Lee SM, Moore S, Wang X, Zhang D, Wu S, Basak P, Wang J, Liu J, Mann RJ, LePage DF, Jiang W, Abid S, Hennig M, Martinez A, Wustman BA, Lockhart DJ, Jain R, Conlon RA, Drumm ML, Hodges CA, Siegwart DJ. Sun Y, et al. Among authors: lockhart dj. Science. 2024 Jun 14;384(6701):1196-1202. doi: 10.1126/science.adk9428. Epub 2024 Jun 13. Science. 2024. PMID: 38870301 Free PMC article.
A quantitative analysis of kinase inhibitor selectivity.
Karaman MW, Herrgard S, Treiber DK, Gallant P, Atteridge CE, Campbell BT, Chan KW, Ciceri P, Davis MI, Edeen PT, Faraoni R, Floyd M, Hunt JP, Lockhart DJ, Milanov ZV, Morrison MJ, Pallares G, Patel HK, Pritchard S, Wodicka LM, Zarrinkar PP. Karaman MW, et al. Among authors: lockhart dj. Nat Biotechnol. 2008 Jan;26(1):127-32. doi: 10.1038/nbt1358. Nat Biotechnol. 2008. PMID: 18183025
Treatment of Fabry's Disease with the Pharmacologic Chaperone Migalastat.
Germain DP, Hughes DA, Nicholls K, Bichet DG, Giugliani R, Wilcox WR, Feliciani C, Shankar SP, Ezgu F, Amartino H, Bratkovic D, Feldt-Rasmussen U, Nedd K, Sharaf El Din U, Lourenco CM, Banikazemi M, Charrow J, Dasouki M, Finegold D, Giraldo P, Goker-Alpan O, Longo N, Scott CR, Torra R, Tuffaha A, Jovanovic A, Waldek S, Packman S, Ludington E, Viereck C, Kirk J, Yu J, Benjamin ER, Johnson F, Lockhart DJ, Skuban N, Castelli J, Barth J, Barlow C, Schiffmann R. Germain DP, et al. Among authors: lockhart dj. N Engl J Med. 2016 Aug 11;375(6):545-55. doi: 10.1056/NEJMoa1510198. N Engl J Med. 2016. PMID: 27509102 Free article. Clinical Trial.
Guideline adherence and survival of patients with candidaemia in Europe: results from the ECMM Candida III multinational European observational cohort study.
Hoenigl M, Salmanton-García J, Egger M, Gangneux JP, Bicanic T, Arikan-Akdagli S, Alastruey-Izquierdo A, Klimko N, Barac A, Özenci V, Meijer EFJ, Khanna N, Bassetti M, Rautemaa-Richardson R, Lagrou K, Adam KM, Akalin EH, Akova M, Arsic Arsenijevic V, Aujayeb A, Blennow O, Bretagne S, Danion F, Denis B, de Jonge NA, Desoubeaux G, Drgona L, Erben N, Gori A, García Rodríguez J, Garcia-Vidal C, Giacobbe DR, Goodman AL, Hamal P, Hammarström H, Toscano C, Lanternier F, Lass-Flörl C, Lockhart DEA, Longval T, Loughlin L, Matos T, Mikulska M, Narayanan M, Martín-Pérez S, Prattes J, Rogers B, Rahimli L, Ruiz M, Roilides E, Samarkos M, Scharmann U, Sili U, Sipahi OR, Sivakova A, Steinmann J, Trauth J, Turhan O, Van Praet J, Vena A, White PL, Willinger B, Tortorano AM, Arendrup MC, Koehler P, Cornely OA; ECMM Candida III Study Group. Hoenigl M, et al. Among authors: lockhart dea. Lancet Infect Dis. 2023 Jun;23(6):751-761. doi: 10.1016/S1473-3099(22)00872-6. Epub 2023 Feb 15. Lancet Infect Dis. 2023. PMID: 37254300 Free article.
Dual SORT LNPs for multi-organ base editing.
Kim M, Song ES, Chen JC, Chatterjee S, Sun Y, Lee SM, Wu S, Patel P, Tian Z, Kantor A, Wustman BA, Lockhart DJ, Siegwart DJ. Kim M, et al. Among authors: lockhart dj. Nat Biotechnol. 2025 Jun 2. doi: 10.1038/s41587-025-02675-z. Online ahead of print. Nat Biotechnol. 2025. PMID: 40457105
Functional characterization of the S. cerevisiae genome by gene deletion and parallel analysis.
Winzeler EA, Shoemaker DD, Astromoff A, Liang H, Anderson K, Andre B, Bangham R, Benito R, Boeke JD, Bussey H, Chu AM, Connelly C, Davis K, Dietrich F, Dow SW, El Bakkoury M, Foury F, Friend SH, Gentalen E, Giaever G, Hegemann JH, Jones T, Laub M, Liao H, Liebundguth N, Lockhart DJ, Lucau-Danila A, Lussier M, M'Rabet N, Menard P, Mittmann M, Pai C, Rebischung C, Revuelta JL, Riles L, Roberts CJ, Ross-MacDonald P, Scherens B, Snyder M, Sookhai-Mahadeo S, Storms RK, Véronneau S, Voet M, Volckaert G, Ward TR, Wysocki R, Yen GS, Yu K, Zimmermann K, Philippsen P, Johnston M, Davis RW. Winzeler EA, et al. Among authors: lockhart dj. Science. 1999 Aug 6;285(5429):901-6. doi: 10.1126/science.285.5429.901. Science. 1999. PMID: 10436161
Oral pharmacological chaperone migalastat compared with enzyme replacement therapy in Fabry disease: 18-month results from the randomised phase III ATTRACT study.
Hughes DA, Nicholls K, Shankar SP, Sunder-Plassmann G, Koeller D, Nedd K, Vockley G, Hamazaki T, Lachmann R, Ohashi T, Olivotto I, Sakai N, Deegan P, Dimmock D, Eyskens F, Germain DP, Goker-Alpan O, Hachulla E, Jovanovic A, Lourenco CM, Narita I, Thomas M, Wilcox WR, Bichet DG, Schiffmann R, Ludington E, Viereck C, Kirk J, Yu J, Johnson F, Boudes P, Benjamin ER, Lockhart DJ, Barlow C, Skuban N, Castelli JP, Barth J, Feldt-Rasmussen U. Hughes DA, et al. Among authors: lockhart dj. J Med Genet. 2017 Apr;54(4):288-296. doi: 10.1136/jmedgenet-2016-104178. Epub 2016 Nov 10. J Med Genet. 2017. PMID: 27834756 Free PMC article. Clinical Trial.
The validation of pharmacogenetics for the identification of Fabry patients to be treated with migalastat.
Benjamin ER, Della Valle MC, Wu X, Katz E, Pruthi F, Bond S, Bronfin B, Williams H, Yu J, Bichet DG, Germain DP, Giugliani R, Hughes D, Schiffmann R, Wilcox WR, Desnick RJ, Kirk J, Barth J, Barlow C, Valenzano KJ, Castelli J, Lockhart DJ. Benjamin ER, et al. Among authors: lockhart dj. Genet Med. 2017 Apr;19(4):430-438. doi: 10.1038/gim.2016.122. Epub 2016 Sep 22. Genet Med. 2017. PMID: 27657681 Free PMC article.
211 results