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Year Number of Results
2011 1
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21 results

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Page 1
Efanesoctocog Alfa Prophylaxis for Children with Severe Hemophilia A.
Malec L, Peyvandi F, Chan AKC, Königs C, Zulfikar B, Yuan H, Simpson M, Álvarez Román MT, Carcao M, Staber JM, Dunn AL, Chou SC, d'Oiron R, Albisetti M, Demissie M, Santagostino E, Yarramaneni A, Wong N, Abad-Franch L, Gunawardena S, Fijnvandraat K; XTEND-Kids Trial Group. Malec L, et al. N Engl J Med. 2024 Jul 18;391(3):235-246. doi: 10.1056/NEJMoa2312611. N Engl J Med. 2024. PMID: 39018533 Clinical Trial.
Treatment of newly diagnosed severe aplastic anemia in children: Evidence-based recommendations.
Shimano KA, Rothman JA, Allen SW, Castillo P, de Jong JLO, Dror Y, Geddis AE, Lau BW, McGuinn C, Narla A, Overholt K, Pereda MA, Sharathkumar A, Sasa G, Nakano TA, Myers K, Gloude NJ, Broglie L, Boklan J. Shimano KA, et al. Among authors: mcguinn c. Pediatr Blood Cancer. 2024 Aug;71(8):e31070. doi: 10.1002/pbc.31070. Epub 2024 May 16. Pediatr Blood Cancer. 2024. PMID: 38757488 Review.
Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant.
George LA, Sullivan SK, Giermasz A, Rasko JEJ, Samelson-Jones BJ, Ducore J, Cuker A, Sullivan LM, Majumdar S, Teitel J, McGuinn CE, Ragni MV, Luk AY, Hui D, Wright JF, Chen Y, Liu Y, Wachtel K, Winters A, Tiefenbacher S, Arruda VR, van der Loo JCM, Zelenaia O, Takefman D, Carr ME, Couto LB, Anguela XM, High KA. George LA, et al. Among authors: mcguinn ce. N Engl J Med. 2017 Dec 7;377(23):2215-2227. doi: 10.1056/NEJMoa1708538. N Engl J Med. 2017. PMID: 29211678 Free PMC article. Clinical Trial.
Diagnostic work-up for severe aplastic anemia in children: Consensus of the North American Pediatric Aplastic Anemia Consortium.
Shimano KA, Narla A, Rose MJ, Gloude NJ, Allen SW, Bergstrom K, Broglie L, Carella BA, Castillo P, de Jong JLO, Dror Y, Geddis AE, Huang JN, Lau BW, McGuinn C, Nakano TA, Overholt K, Rothman JA, Sharathkumar A, Shereck E, Vlachos A, Olson TS, Bertuch AA, Wlodarski MW, Shimamura A, Boklan J. Shimano KA, et al. Among authors: mcguinn c. Am J Hematol. 2021 Nov 1;96(11):1491-1504. doi: 10.1002/ajh.26310. Epub 2021 Aug 20. Am J Hematol. 2021. PMID: 34342889 Free article.
Congenital fibrinogen disorders: a retrospective clinical and genetic analysis of the Prospective Rare Bleeding Disorders Database.
Mohsenian S, Palla R, Menegatti M, Cairo A, Lecchi A, Casini A, Neerman-Arbez M, Asselta R, Scardo S, Siboni SM, Blatny J, Zapletal O, Schved JF, Giansily-Blaizot M, Halimeh S, Daoud MA, Platokouki H, Pergantou H, Schutgens REG, Van Haaften-Spoor M, Brons P, Laros-van Gorkom B, Van Pinxten E, Borhany M, Fatima N, Mikovic D, Saracevic M, Özdemir GN, Ay Y, Makris M, Lockley C, Mumford A, Harvey A, Austin S, Shapiro A, Williamson A, McGuinn C, Goldberg I, De Moerloose P, Peyvandi F. Mohsenian S, et al. Among authors: mcguinn c. Blood Adv. 2024 Mar 26;8(6):1392-1404. doi: 10.1182/bloodadvances.2023012186. Blood Adv. 2024. PMID: 38286442 Free PMC article.
Haemophilia: factoring in new therapies.
Fassel H, McGuinn C. Fassel H, et al. Among authors: mcguinn c. Br J Haematol. 2021 Sep;194(5):835-850. doi: 10.1111/bjh.17580. Epub 2021 Jul 28. Br J Haematol. 2021. PMID: 34322873 Review.
Fidanacogene Elaparvovec for Hemophilia B - A Multiyear Follow-up Study.
Rasko JEJ, Samelson-Jones BJ, George LA, Giermasz A, Ducore JM, Teitel JM, McGuinn CE, High KA, de Jong YP, Chhabra A, O'Brien A, Smith LM, Winburn I, Rupon J. Rasko JEJ, et al. Among authors: mcguinn ce. N Engl J Med. 2025 Apr 17;392(15):1508-1517. doi: 10.1056/NEJMoa2307159. N Engl J Med. 2025. PMID: 40239068 Clinical Trial.
Treatment of relapsed/refractory severe aplastic anemia in children: Evidence-based recommendations.
Shimano KA, Sasa G, Broglie L, Gloude NJ, Myers K, Nakano TA, Sharathkumar A, Rothman JA, Pereda MA, Overholt K, Narla A, McGuinn C, Lau BW, Geddis AE, Dror Y, de Jong JLO, Castillo P, Allen SW, Boklan J. Shimano KA, et al. Among authors: mcguinn c. Pediatr Blood Cancer. 2024 Aug;71(8):e31075. doi: 10.1002/pbc.31075. Epub 2024 May 19. Pediatr Blood Cancer. 2024. PMID: 38764170 Review.
21 results