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Table representation of search results timeline featuring number of search results per year.
| Year | Number of Results |
|---|---|
| 2024 | 2 |
| 2025 | 1 |
| 2026 | 0 |
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Evaluating the efficacy and safety of pozelimab in patients with CD55 deficiency with hyperactivation of complement, angiopathic thrombosis, and protein-losing enteropathy disease: an open-label phase 2 and 3 study.
Lancet. 2024 Feb 17;403(10427):645-656. doi: 10.1016/S0140-6736(23)02358-9. Epub 2024 Jan 23.
Lancet. 2024.
PMID: 38278170
Free PMC article.
Clinical Trial.
The patient experience of CHAPLE disease: results from interviews conducted as part of a clinical trial for an ultra-rare condition.
Litcher-Kelly L, Ozen A, Ollis S, Feldman HB, Yaworsky A, Medrano P, Chongsrisawat V, Perlee L, Walker M, Pradeep S, Turner-Bowker DM, Kurolap A, Adiv OE, Lenardo MJ, Harari OA, Jalbert JJ.
Litcher-Kelly L, et al.
Orphanet J Rare Dis. 2025 Feb 11;20(1):68. doi: 10.1186/s13023-024-03436-y.
Orphanet J Rare Dis. 2025.
PMID: 39934837
Free PMC article.
Clinical Trial.
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Pozelimab for CHAPLE disease: results from in-trial interviews and clinical outcome assessments.
Litcher-Kelly L, Ozen A, Ollis S, Feldman HB, Yaworsky A, Medrano P, Chongsrisawa V, Brackin T, Perlee L, Walker M, Pradeep S, Lenardo MJ, Harari OA, Jalbert JJ.
Litcher-Kelly L, et al.
Orphanet J Rare Dis. 2024 Aug 8;19(1):290. doi: 10.1186/s13023-024-03277-9.
Orphanet J Rare Dis. 2024.
PMID: 39118150
Free PMC article.
Clinical Trial.
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