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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
1968 1
1969 2
1970 1
1972 1
1986 1
1990 1
1991 2
1992 1
1993 1
1994 1
1996 2
1998 1
1999 2
2000 2
2001 2
2002 4
2003 2
2004 6
2005 10
2006 7
2007 5
2008 12
2009 8
2010 10
2011 13
2012 8
2013 4
2014 7
2015 6
2016 8
2017 9
2018 8
2019 8
2020 4
2021 9
2022 11
2023 8
2024 7
2025 6

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179 results

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Page 1
Gene therapy for hemophilia.
Nathwani AC. Nathwani AC. Hematology Am Soc Hematol Educ Program. 2022 Dec 9;2022(1):569-578. doi: 10.1182/hematology.2022000388. Hematology Am Soc Hematol Educ Program. 2022. PMID: 36485127 Free PMC article. Review.
Gene therapy for hemophilia.
Nathwani AC. Nathwani AC. Hematology Am Soc Hematol Educ Program. 2019 Dec 6;2019(1):1-8. doi: 10.1182/hematology.2019000007. Hematology Am Soc Hematol Educ Program. 2019. PMID: 31808868 Free PMC article. Review.
Adenovirus-associated virus vector-mediated gene transfer in hemophilia B.
Nathwani AC, Tuddenham EG, Rangarajan S, Rosales C, McIntosh J, Linch DC, Chowdary P, Riddell A, Pie AJ, Harrington C, O'Beirne J, Smith K, Pasi J, Glader B, Rustagi P, Ng CY, Kay MA, Zhou J, Spence Y, Morton CL, Allay J, Coleman J, Sleep S, Cunningham JM, Srivastava D, Basner-Tschakarjan E, Mingozzi F, High KA, Gray JT, Reiss UM, Nienhuis AW, Davidoff AM. Nathwani AC, et al. N Engl J Med. 2011 Dec 22;365(25):2357-65. doi: 10.1056/NEJMoa1108046. Epub 2011 Dec 10. N Engl J Med. 2011. PMID: 22149959 Free PMC article. Clinical Trial.
Adeno-associated virus gene therapy prevents progression of kidney disease in genetic models of nephrotic syndrome.
Ding WY, Kuzmuk V, Hunter S, Lay A, Hayes B, Beesley M, Rollason R, Hurcombe JA, Barrington F, Masson C, Cathery W, May C, Tuffin J, Roberts T, Mollet G, Chu CJ, McIntosh J, Coward RJ, Antignac C, Nathwani A, Welsh GI, Saleem MA. Ding WY, et al. Among authors: nathwani a. Sci Transl Med. 2023 Aug 9;15(708):eabc8226. doi: 10.1126/scitranslmed.abc8226. Epub 2023 Aug 9. Sci Transl Med. 2023. PMID: 37556557
FLT201, a novel liver-directed AAV gene therapy candidate for Gaucher disease type 1.
Comper F, Miranda CJ, Liou B, Dodev T, Jeyakumar JM, Canavese M, Cocita C, Khoshrou K, Tiscornia G, Chisari E, Stotter E, Shehu E, Sridharan S, Yu IM, Pandya J, Khinder J, Northcott N, Kalcheva P, Correia S, Sun Y, Dane AP, Sheridan R, Nathwani AC, Corbau R. Comper F, et al. Among authors: nathwani ac. Mol Ther. 2025 Aug 6;33(8):3789-3807. doi: 10.1016/j.ymthe.2025.05.003. Epub 2025 May 7. Mol Ther. 2025. PMID: 40340248 Free article.
Liver Gene Therapy.
Nathwani AC, McIntosh J, Sheridan R. Nathwani AC, et al. Hum Gene Ther. 2022 Sep;33(17-18):879-888. doi: 10.1089/hum.2022.169. Hum Gene Ther. 2022. PMID: 36082993 Review.
Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia B.
Reiss UM, Davidoff AM, Tuddenham EGD, Chowdary P, McIntosh J, Muczynski V, Journou M, Simini G, Ireland L, Mohamed S, Riddell A, Pie AJ, Hall A, Quaglia A, Mangles S, Mahlangu J, Haley K, Recht M, Shen YM, Halka KG, Fortner G, Morton CL, Gu Z, Hayden RT, Neufeld EJ, Okhomina VI, Kang G, Nathwani AC. Reiss UM, et al. Among authors: nathwani ac. N Engl J Med. 2025 Jun 12;392(22):2226-2234. doi: 10.1056/NEJMoa2414783. N Engl J Med. 2025. PMID: 40499172 Free PMC article. Clinical Trial.
Preclinical evaluation of FLT190, a liver-directed AAV gene therapy for Fabry disease.
Jeyakumar JM, Kia A, Tam LCS, McIntosh J, Spiewak J, Mills K, Heywood W, Chisari E, Castaldo N, Verhoef D, Hosseini P, Kalcheva P, Cocita C, Miranda CJ, Canavese M, Khinder J, Rosales C, Hughes D, Sheridan R, Corbau R, Nathwani A. Jeyakumar JM, et al. Among authors: nathwani a. Gene Ther. 2023 Jun;30(6):487-502. doi: 10.1038/s41434-022-00381-y. Epub 2023 Jan 11. Gene Ther. 2023. PMID: 36631545 Free PMC article.
Phase 1-2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B.
Chowdary P, Shapiro S, Makris M, Evans G, Boyce S, Talks K, Dolan G, Reiss U, Phillips M, Riddell A, Peralta MR, Quaye M, Patch DW, Tuddenham E, Dane A, Watissée M, Long A, Nathwani A. Chowdary P, et al. Among authors: nathwani a. N Engl J Med. 2022 Jul 21;387(3):237-247. doi: 10.1056/NEJMoa2119913. N Engl J Med. 2022. PMID: 35857660 Free article. Clinical Trial.
179 results