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Did you mean sallach jb (38 results)?
Safety and Efficacy of DTX401, an AAV8-Mediated Liver-Directed Gene Therapy, in Adults With Glycogen Storage Disease Type I a (GSDIa).
Weinstein DA, Derks TG, Rodriguez-Buritica DF, Ahmad A, Couce ML, Mitchell JJ, Riba-Wolman R, Mount M, Sallago JB, Ross KM, van der Klauw MM, de Boer F, van der Schaaf C, Saavedra H, Martínez-Olmos M, Atanga E, Hosseini A, Mitragotri D, Crombez E. Weinstein DA, et al. Among authors: sallago jb. J Inherit Metab Dis. 2025 Mar;48(2):e70014. doi: 10.1002/jimd.70014. J Inherit Metab Dis. 2025. PMID: 40064185 Free PMC article. Clinical Trial.
Person-centered outcomes for liver glycogen storage diseases: Development of an international consensus-based standard outcome set.
Overduin RJ, Haijer-Schreuder AB, Withaar FK, Grünert SC, LaFreniere J, Contreras EL, Temkin GW, Stone-Schneider B, Vanneste F, Dekker H, Fokkert-Wilts MJ, van der Klauw MM, Weinstein DA, Rossi A, Derks TGJ; GSD Value Consortium. Overduin RJ, et al. Genet Med. 2025 Sep 23;27(12):101589. doi: 10.1016/j.gim.2025.101589. Online ahead of print. Genet Med. 2025. PMID: 41014099 Free article.