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Page 1
Aficamten for Symptomatic Obstructive Hypertrophic Cardiomyopathy.
Maron MS, Masri A, Nassif ME, Barriales-Villa R, Arad M, Cardim N, Choudhury L, Claggett B, Coats CJ, Düngen HD, Garcia-Pavia P, Hagège AA, Januzzi JL, Lee MMY, Lewis GD, Ma CS, Michels M, Olivotto I, Oreziak A, Owens AT, Spertus JA, Solomon SD, Tfelt-Hansen J, van Sinttruije M, Veselka J, Watkins H, Jacoby DL, Heitner SB, Kupfer S, Malik FI, Meng L, Wohltman A, Abraham TP; SEQUOIA-HCM Investigators. Maron MS, et al. N Engl J Med. 2024 May 30;390(20):1849-1861. doi: 10.1056/NEJMoa2401424. Epub 2024 May 13. N Engl J Med. 2024. PMID: 38739079 Clinical Trial.
Aficamten and Cardiopulmonary Exercise Test Performance: A Substudy of the SEQUOIA-HCM Randomized Clinical Trial.
Lee MMY, Masri A, Nassif ME, Barriales-Villa R, Abraham TP, Claggett BL, Coats CJ, Gimeno JR, Kulac IJ, Landsteiner I, Ma C, Maron MS, Olivotto I, Owens AT, Solomon SD, Veselka J, Jacoby DL, Heitner SB, Kupfer S, Malik FI, Meng L, Wohltman A, Lewis GD; SEQUOIA-HCM Investigators. Lee MMY, et al. JAMA Cardiol. 2024 Nov 1;9(11):990-1000. doi: 10.1001/jamacardio.2024.2781. JAMA Cardiol. 2024. PMID: 39230885 Free PMC article. Clinical Trial.
A novel tool for arrhythmic risk stratification in desmoplakin gene variant carriers.
Carrick RT, Gasperetti A, Protonotarios A, Murray B, Laredo M, van der Schaaf I, Dooijes D, Syrris P, Cannie D, Tichnell C, Gilotra NA, Cappelletto C, Medo K, Saguner AM, Duru F, Hylind RJ, Abrams DJ, Lakdawala NK, Cadrin-Tourigny J, Targetti M, Olivotto I, Graziosi M, Cox M, Biagini E, Charron P, Compagnucci P, Casella M, Conte G, Tondo C, Yazdani M, Ware JS, Prasad SK, Calò L, Smith ED, Helms AS, Hespe S, Ingles J, Tandri H, Ader F, Peretto G, Peters S, Horton A, Yao J, Schulze-Bahr E, Dittman S, Carruth ED, Young K, Qureshi M, Haggerty C, Parikh VN, Taylor M, Mestroni L, Wilde A, Sinagra G, Merlo M, Gandjbakhch E, van Tintelen JP, Te Riele ASJM, Elliott P, Calkins H, Wu KC, James CA. Carrick RT, et al. Among authors: targetti m. Eur Heart J. 2024 Aug 21;45(32):2968-2979. doi: 10.1093/eurheartj/ehae409. Eur Heart J. 2024. PMID: 39011630 Free PMC article.
Clinical features and outcomes in carriers of pathogenic desmoplakin variants.
Gasperetti A, Carrick RT, Protonotarios A, Murray B, Laredo M, van der Schaaf I, Lekanne RH, Syrris P, Cannie D, Tichnell C, Cappelletto C, Gigli M, Medo K, Saguner AM, Duru F, Gilotra NA, Zimmerman S, Hylind R, Abrams DJ, Lakdawala NK, Cadrin-Tourigny J, Targetti M, Olivotto I, Graziosi M, Cox M, Biagini E, Charron P, Casella M, Tondo C, Yazdani M, Ware JS, Prasad SK, Calò L, Smith ED, Helms AS, Hespe S, Ingles J, Tandri H, Ader F, Peretto G, Peters S, Horton A, Yao J, Dittmann S, Schulze-Bahr E, Qureshi M, Young K, Carruth ED, Haggerty C, Parikh VN, Taylor M, Mestroni L, Wilde A, Sinagra G, Merlo M, Gandjbakhch E, van Tintelen JP, Te Riele ASJM, Elliott PM, Calkins H, James CA. Gasperetti A, et al. Among authors: targetti m. Eur Heart J. 2025 Jan 21;46(4):362-376. doi: 10.1093/eurheartj/ehae571. Eur Heart J. 2025. PMID: 39288222 Free PMC article.
Aficamten or Metoprolol Monotherapy for Obstructive Hypertrophic Cardiomyopathy.
Garcia-Pavia P, Maron MS, Masri A, Merkely B, Nassif ME, Peña-Peña ML, Barriales-Villa R, Bilen O, Burroughs M, Claggett B, Costabel JP, Correia EB, Dybro AM, Elliott P, Hegde SM, Lakdawala NK, Lewis GD, Mann A, Miao ZM, Nair A, Poulsen SH, Reant P, Schulze PC, Solomon SD, Wang A, Sohn R, Berhane I, Heitner SB, Jacoby DL, Kupfer S, Malik FI, Wohltman A, Fifer MA; MAPLE-HCM Investigators. Garcia-Pavia P, et al. N Engl J Med. 2025 Sep 11;393(10):949-960. doi: 10.1056/NEJMoa2504654. Epub 2025 Aug 30. N Engl J Med. 2025. PMID: 40888697 Clinical Trial.
Diagnostic delay in arrhythmogenic cardiomyopathy.
Tini G, Graziosi M, Musumeci B, Targetti M, Russo D, Parisi V, Argirò A, Ditaranto R, Leone O, Autore C, Olivotto I, Biagini E. Tini G, et al. Among authors: targetti m. Eur J Prev Cardiol. 2023 Sep 20;30(13):1315-1322. doi: 10.1093/eurjpc/zwad058. Eur J Prev Cardiol. 2023. PMID: 36848329
The Diagnostic Value of the 12-Lead ECG in Arrhythmogenic Left Ventricular Cardiomyopathy: Novel ECG Signs.
Calò L, Crescenzi C, Martino A, Casella M, Romeo F, Cappelletto C, Bressi E, Panattoni G, Stolfo D, Targetti M, Toso E, Musumeci MB, Tini G, Ciabatti M, Stefanini M, Silvetti E, Stazi A, Danza ML, Rebecchi M, Canestrelli S, Fedele E, Lanzillo C, Fusco A, Sangiuolo FC, Oliviero G, Radesich C, Perotto M, Pieroni M, Golia P, Mango R, Gasperetti A, Autore C, Merlo M, de Ruvo E, Russo AD, Olivotto I, Sinagra G, Gaita F. Calò L, et al. Among authors: targetti m. JACC Clin Electrophysiol. 2023 Dec;9(12):2615-2627. doi: 10.1016/j.jacep.2023.08.020. Epub 2023 Sep 27. JACC Clin Electrophysiol. 2023. PMID: 37768253 Free article. Review.
Long-Term Arrhythmic Follow-Up and Risk Stratification of Patients With Desmoplakin-Associated Arrhythmogenic Right Ventricular Cardiomyopathy.
Gasperetti A, Carrick R, Protonotarios A, Laredo M, van der Schaaf I, Syrris P, Murray B, Tichnell C, Cappelletto C, Gigli M, Medo K, Crabtree P, Saguner AM, Duru F, Hylind R, Abrams D, Lakdawala NK, Massie C, Cadrin-Tourigny J, Targetti M, Olivotto I, Graziosi M, Cox M, Biagini E, Charron P, Casella M, Tondo C, Yazdani M, Ware JS, Prasad S, Calò L, Smith E, Helms A, Hespe S, Ingles J, Tandri H, Ader F, Mestroni L, Wilde A, Merlo M, Gandjbakhch E, Calkins H, Te Riele ASJM, Peter van Tintelen J, Elliot P, James CA. Gasperetti A, et al. Among authors: targetti m. JACC Adv. 2024 Feb 2;3(3):100832. doi: 10.1016/j.jacadv.2024.100832. eCollection 2024 Mar. JACC Adv. 2024. PMID: 38938828 Free PMC article.
Prognostic Role of Myocarditis-Like Episodes and Their Treatment in Patients With Pathogenic Desmoplakin Variants.
Gasperetti A, Muller SA, Peretto G, Asatryan B, Protonotarios A, Laredo M, Tarlet PY, Syrris P, Carrick RT, Murray B, Tichnell C, Scheel P, Gigli M, Yap SC, Pilichou K, Basso C, Medo K, Jason M, Rossi VA, Saguner AM, Duru F, Abrams D, Cadrin-Tourigny J, Targetti M, Pieroni M, Graziosi M, Biagini E, Charron P, Cox M, Casella M, Tondo C, Ware JS, Prasad SK, Calò L, Smith E, Ingles J, Tandri H, Ader F, Peters S, Zentner D, Russo J, Ravaro S, Crotti L, Dittmann S, Shulze-Bahr E, Carruth ED, Krysov VA, Parikh VN, Conte G, Wilde A, van Tintelen JP, Te Riele ASJM, Sinagra G, Mestroni L, Taylor M, Merlo M, Adamo L, Calkins H, Bauce B, Arbelo E, Elliott PM, Gandjbakhch E, Lakdawala N, Helms A, James CA, Gilotra NA. Gasperetti A, et al. Among authors: targetti m. Circulation. 2025 Aug 20. doi: 10.1161/CIRCULATIONAHA.125.073919. Online ahead of print. Circulation. 2025. PMID: 40832715
40 results