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1993 1
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2009 6
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94 results

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Page 1
Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease.
Musunuru K, Grandinette SA, Wang X, Hudson TR, Briseno K, Berry AM, Hacker JL, Hsu A, Silverstein RA, Hille LT, Ogul AN, Robinson-Garvin NA, Small JC, McCague S, Burke SM, Wright CM, Bick S, Indurthi V, Sharma S, Jepperson M, Vakulskas CA, Collingwood M, Keogh K, Jacobi A, Sturgeon M, Brommel C, Schmaljohn E, Kurgan G, Osborne T, Zhang H, Kinney K, Rettig G, Barbosa CJ, Semple SC, Tam YK, Lutz C, George LA, Kleinstiver BP, Liu DR, Ng K, Kassim SH, Giannikopoulos P, Alameh MG, Urnov FD, Ahrens-Nicklas RC. Musunuru K, et al. Among authors: urnov fd. N Engl J Med. 2025 Jun 12;392(22):2235-2243. doi: 10.1056/NEJMoa2504747. Epub 2025 May 15. N Engl J Med. 2025. PMID: 40373211
A roadmap for affordable genetic medicines.
Kliegman M, Zaghlula M, Abrahamson S, Esensten JH, Wilson RC, Urnov FD, Doudna JA. Kliegman M, et al. Among authors: urnov fd. Nature. 2024 Oct;634(8033):307-314. doi: 10.1038/s41586-024-07800-7. Epub 2024 Jul 17. Nature. 2024. PMID: 39019069 Free article. Review.
Imagine CRISPR cures.
Urnov FD. Urnov FD. Mol Ther. 2021 Nov 3;29(11):3103-3106. doi: 10.1016/j.ymthe.2021.10.019. Epub 2021 Oct 28. Mol Ther. 2021. PMID: 34710352 Free PMC article. No abstract available.
CRISPR-Cas9 can cause chromothripsis.
Urnov FD. Urnov FD. Nat Genet. 2021 Jun;53(6):768-769. doi: 10.1038/s41588-021-00881-4. Nat Genet. 2021. PMID: 34103715 No abstract available.
Enhancing pediatric access to cell and gene therapies.
Mackall CL, Bollard CM, Goodman N, Carr C, Gardner R, Rouce R, Sotillo E, Stoner R, Urnov FD, Wayne AS, Park J, Kohn DB. Mackall CL, et al. Among authors: urnov fd. Nat Med. 2024 Jul;30(7):1836-1846. doi: 10.1038/s41591-024-03035-1. Epub 2024 Jun 17. Nat Med. 2024. PMID: 38886624 Review.
Functional footprinting of regulatory DNA.
Vierstra J, Reik A, Chang KH, Stehling-Sun S, Zhou Y, Hinkley SJ, Paschon DE, Zhang L, Psatha N, Bendana YR, O'Neil CM, Song AH, Mich AK, Liu PQ, Lee G, Bauer DE, Holmes MC, Orkin SH, Papayannopoulou T, Stamatoyannopoulos G, Rebar EJ, Gregory PD, Urnov FD, Stamatoyannopoulos JA. Vierstra J, et al. Among authors: urnov fd. Nat Methods. 2015 Oct;12(10):927-30. doi: 10.1038/nmeth.3554. Epub 2015 Aug 31. Nat Methods. 2015. PMID: 26322838 Free PMC article.
94 results